Stem Cell Therapy in Lysosomal Storage Diseases /
| Autor Corporativo: | |
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| Otros Autores: | , |
| Formato: | eBook |
| Lenguaje: | English |
| Publicado: |
New York, NY :
Springer New York : Imprint: Humana,
2013.
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| Edición: | 1st ed. 2013. |
| Colección: | Stem Cell Biology and Regenerative Medicine,
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| Materias: |
Tabla de Contenidos:
- 1. Lysosomal Diseases and Therapeutic Options: An Overview
- 2. Alternative Treatment Options: Enzyme Replacement and Small Molecule Therapies
- 3. Hematopoietic Cell Transplantation in Inborn Errors of Metabolism
- 4. Allogeneic Hematopoietic Stem Cell Transplantation in Lysosomal Storage Disorders: Long Term Neurodevelopmental and Somatic Outcome
- 5. Hematopoietic Stem Cell Gene Therapy for Lysosomal Storage Disorders: Expected Benefits and Limitations
- 6. Alternative Future Therapies for Lysosomal Storage Diseases: Embryonic Stem Cell- and Induced Pluripotent Stem Cell Therapy
- 7. New Directions and Conclusions.