Retinal Gene Therapy : Methods and Protocols /
| Autor Corporativo: | |
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| Otros Autores: | , |
| Formato: | eBook |
| Lenguaje: | English |
| Publicado: |
New York, NY :
Springer New York : Imprint: Humana,
2018.
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| Edición: | 1st ed. 2018. |
| Colección: | Methods in Molecular Biology,
1715 |
| Materias: |
Tabla de Contenidos:
- Small Scale Production of Recombinant Adeno-Associated Viral Vectors for Gene Delivery to the Nervous System
- Small and Micro-Scale Recombinant Adeno-Associated Virus Production and Purification for Ocular Gene Therapy Applications
- Design and Development of AAV-Based Gene Supplementation Therapies for Achromatopsia and Retinitis Pigmentosa
- Development of Multigenic Lentiviral Vectors for Cell-Specific Expression of Antiangiogenic miRNAs and Protein Factors
- Design and In Vitro Use of Antisense Oligonucleotides to Correct Pre-mRNA Splicing Defects in Inherited Retinal Dystrophies
- Three-Dimensional Co-Culture Bioassay for Screening of Retinal Gene Delivery Systems
- Retinal Gene Therapy for Choroideremia: In Vitro Testing for Gene Augmentation Using an Adeno-Associated Viral (AAV) Vector
- In Vivo Electroporation of Developing Mouse Retina
- Methods for In Vivo CRISPR/Cas Editing of the Adult Murine Retina
- AAV Gene Augmentation Therapy for CRB1-Associated Retinitis Pigmentosa
- Dual AAV Vectors for Stargardt Disease
- Optogenetic Retinal Gene Therapy with the Light Gated GPCR Vertebrate Rhodopsin
- CRISPR Repair Reveals Causative Mutation in a Preclinical Model of Retinitis Pigmentosa: A Brief Methodology
- In-Depth Functional Analysis of Rodents by Full-Field Electroretinography
- Advanced Ocular Injection Techniques for Therapy Approaches
- Neutralizing Antibodies Against Adeno-Associated Virus (AAV): Measurement and Influence on Retinal Gene Delivery
- Screening for Neutralizing Antibodies against Natural and Engineered AAV Capsids in Non-Human Primate Retinas
- Subretinal and Intravitreal Retinal Injections in Monkeys
- Production of iPS-derived Human Retinal Organoids for Use in Transgene Expression Assays
- AAV Serotype Testing on Cultured Human Donor Retinal Explants
- Human Retinal Explant Culture for Ex-Vivo Validation of AAV Gene Therapy
- Visual Acuity Testing Before and After Intravitreal Injection of rAAV2- ND4 in Patients
- Recording and Analysis of the Human Clinical Electroretinogram
- Recording and Analysis of Goldmann Kinetic Visual Fields
- Measuring Central Retinal Sensitivity Using Microperimetry
- Inspection of the Human Retina by Optical Coherence Tomography
- Vector Shedding and Immunogenicity Sampling for Retinal Gene Therapy.