Stem Cell Therapy in Lysosomal Storage Diseases /
| Corporate Author: | |
|---|---|
| Other Authors: | , |
| Format: | eBook |
| Language: | English |
| Published: |
New York, NY :
Springer New York : Imprint: Humana,
2013.
|
| Edition: | 1st ed. 2013. |
| Series: | Stem Cell Biology and Regenerative Medicine,
|
| Subjects: |
Table of Contents:
- 1. Lysosomal Diseases and Therapeutic Options: An Overview
- 2. Alternative Treatment Options: Enzyme Replacement and Small Molecule Therapies
- 3. Hematopoietic Cell Transplantation in Inborn Errors of Metabolism
- 4. Allogeneic Hematopoietic Stem Cell Transplantation in Lysosomal Storage Disorders: Long Term Neurodevelopmental and Somatic Outcome
- 5. Hematopoietic Stem Cell Gene Therapy for Lysosomal Storage Disorders: Expected Benefits and Limitations
- 6. Alternative Future Therapies for Lysosomal Storage Diseases: Embryonic Stem Cell- and Induced Pluripotent Stem Cell Therapy
- 7. New Directions and Conclusions.